CRISPR Medicine

Helex Bio

Company Type: Therapeutic development

Main focus: Developing gene-editing based therapeutics to treat genetic kidney diseases

Company stage: Pre-clinical

Diseases: Autosomal dominant polycystic kidney disease, inherited retinal dystrophies, and other genetic disorders

Genome-editing tool: CRISPR-Cas9

Funding stage: Private

Location: New York, New York, USA

Website: www.helex.bio

Pipeline: www.helex.bio/technology

Partners:


Helex Bio is a pre-clinical biotechnology company focused on advancing safer in vivo gene-editing therapies to treat genetic kidney diseases and other genetic disorders. The company has developed a proprietary lipid nanoparticle delivery system for safe and effective delivery to the kidneys, as well as EPIC-Cure™, a proprietary drug design platform. EPIC-Cure™ seeks to provide a genome-encompassing, data-driven gene-editing drug design for higher precision of editing.

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