CRISPR CLINICAL TRIALS
Medicine is changing.
New CRISPR gene editing clinical studies are rapidly emerging and we think a comprehensive overview is valuable to help keep track of them all.
CRISPR is the hot new rapidly rising gene editing tool but we also include clinical trials of other gene editing modalities like the Zinc Finger Nucleases, TALENs, MegaTALS, CAS-CLOVER, MegaNucleases and any new variants that will be out there in the future. We will keep updating our overview.
Check already now the world's-first clinical trial for a CRISPR-Cas3 phage therapy for treatment of urinary tract infections, developed by Locus BioSciences and get all the details about their unique technology from this interview with VP, Business Development, Joseph Nixon.
The clinical trials are arranged in the following areas:
- Antibacterials
- Blood
- Cancer
- Eye
- Metabolic disorders
- Other genetic conditions
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Autoimmune diseases
Bacterial diseases
Cardiovascular diseases
Sponsors:
CRISPR Therapeutics AG

Sponsors:
Verve Therapeutics, Inc.

Haematological malignancies (blood cancers)
Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust

Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.

Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.

Sponsors:
The First Affiliated Hospital of Nanjing Medical University

Sponsors:
Institut de Recherches Internationales Servier

Sponsors:
Chinese PLA General Hospital

Sponsors:
German Cancer Research Center

Sponsors:
Fate Therapeutics, Inc

Sponsors:
Caribou Biosciences, Inc.

Sponsors:
Great Ormond Street Hospital for Children NHS Trust

Sponsors:
Institut de Recherches Internationales Servier

Sponsors:
Cellectis S.A.

Sponsors:
Xuzhou Medical University

Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust

Sponsors:
Fate Therapeutics

Sponsors:
Bioray Laboratories - Shanghai Bangyao Biotechnology Co., Ltd.

Sponsors:
Third Military Medical University

Sponsors:
Xijing Hospital, The Fourth Military Medical University

Sponsors:
Caribou Biosciences, Inc.

Sponsors:
Bioray Laboratories

Sponsors:
Huazhong University of Science and Technology

Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.

Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.

Sponsors:
Wugen inc.

Sponsors:
Xinqiao Hospital of Chongqing, Second Affiliated Hospital of the Army Medical University, Hematology Department

Sponsors:
Great Ormond Street Hospital

Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust

Sponsors:
Beam Therapeutics Inc.

Haemoglobinopathies
Sponsors:
Sangamo Therapeutics

Sponsors:
Vertex Pharmaceuticals Incorporated

Sponsors:
923rd Hospital of The People's Liberation Army

Sponsors:
The First Affiliated Hospital, Guangxi Medical University

Sponsors:
Institute of Hematology and Blood Diseases Hospital

Sponsors:
Institute of Hematology & Blood Diseases Hospital, China

Sponsors:
Children's Hospital of Fudan University

Sponsors:
CorrectSequence Therapeutics Co., Ltd

Haemophilia
Hereditary amyloidosis
Sponsors:
Intellia Therapeutics

Immunodeficiencies
Sponsors:
National Institute of Allergy and Infectious Diseases (NIAID)

Inherited eye diseases
Sponsors:
HuidaGene Therapeutics Co., Ltd.

Sponsors:
HuidaGene Therapeutics Co., Ltd.

Metabolic disorders
Muscular dystrophies
Neurological disease
Sponsors:
Wave Life Sciences Ltd.

Sponsors:
Wave Life Sciences Ltd.

Solid cancers
Sponsors:
Yang Yang, MD, PhD, MSCR, The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical School

Sponsors:
Huazhong University of Science and Technology

Sponsors:
Huazhong University of Science and Technology

Sponsors:
First Affiliated Hospital, Sun Yat-Sen University

Sponsors:
First Affiliated Hospital of Guangdong Pharmaceutical University

Sponsors:
The First Affiliated Hospital of Guangdong Pharmaceutical University

Viral diseases
Sponsors:
Affiliated Hospital to Academy of Military Medical Sciences

Sponsors:
Mahmoud Ramadan mohamed Elkazzaz

Other rare inherited blood disorders
Sponsors:
Shanghai Children's Medical Center

Other rare inherited disorders
Long-term follow-up (LTFU) studies
Sponsors:
Precision BioSciences, Inc.

Sponsors:
Editas Medicine, Inc.

Sponsors:
Vertex Pharmaceuticals

Sponsors:
Sangamo Therapeutics
