CRISPR CLINICAL TRIALS
Medicine is changing.
New CRISPR gene editing clinical studies are rapidly emerging and we think a comprehensive overview is valuable to help keep track of them all.
CRISPR is the hot new rapidly rising gene editing tool but we also include clinical trials of other gene editing modalities like the Zinc Finger Nucleases, TALENs, MegaTALS, CAS-CLOVER, MegaNucleases and any new variants that will be out there in the future. We will keep updating our overview.
Check already now the world's-first clinical trial for a CRISPR-Cas3 phage therapy for treatment of urinary tract infections, developed by Locus BioSciences and get all the details about their unique technology from this interview with VP, Business Development, Joseph Nixon.
The clinical trials are arranged in the following areas:
- Antibacterials
- Blood
- Cancer
- Eye
- Metabolic disorders
- Other genetic conditions
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Autoimmune diseases
Bacterial diseases
Cardiovascular diseases
Sponsors:
CRISPR Therapeutics AG
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Sponsors:
Verve Therapeutics, Inc.
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Haematological malignancies (blood cancers)
Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust
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Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.
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Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.
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Sponsors:
The First Affiliated Hospital of Nanjing Medical University
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Sponsors:
Institut de Recherches Internationales Servier
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Sponsors:
German Cancer Research Center
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Sponsors:
Fate Therapeutics, Inc
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Sponsors:
Caribou Biosciences, Inc.
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Sponsors:
Great Ormond Street Hospital for Children NHS Trust
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Sponsors:
Institut de Recherches Internationales Servier
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Sponsors:
Cellectis S.A.
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Sponsors:
Xuzhou Medical University
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Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust
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Sponsors:
Fate Therapeutics
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Sponsors:
Bioray Laboratories - Shanghai Bangyao Biotechnology Co., Ltd.
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Sponsors:
Third Military Medical University
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Sponsors:
Xijing Hospital, The Fourth Military Medical University
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Sponsors:
Caribou Biosciences, Inc.
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Sponsors:
Huazhong University of Science and Technology
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Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.
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Sponsors:
Bioray Laboratories - Bangyao Biotechnology Co., Ltd.
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Sponsors:
Wugen inc.
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Sponsors:
Xinqiao Hospital of Chongqing, Second Affiliated Hospital of the Army Medical University, Hematology Department
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Sponsors:
Great Ormond Street Hospital
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Sponsors:
Great Ormond Street Hospital for Children NHS Foundation Trust
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Sponsors:
Beam Therapeutics Inc.
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Haemoglobinopathies
Sponsors:
Sangamo Therapeutics
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Sponsors:
Vertex Pharmaceuticals Incorporated
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Sponsors:
923rd Hospital of The People's Liberation Army
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Sponsors:
The First Affiliated Hospital, Guangxi Medical University
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Sponsors:
Institute of Hematology and Blood Diseases Hospital
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Sponsors:
Institute of Hematology & Blood Diseases Hospital, China
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Haemophilia
Hereditary amyloidosis
Immunodeficiencies
Sponsors:
National Institute of Allergy and Infectious Diseases (NIAID)
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Inherited eye diseases
Sponsors:
HuidaGene Therapeutics Co., Ltd.
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Metabolic disorders
Muscular dystrophies
Neurological disease
Sponsors:
Wave Life Sciences Ltd.
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Sponsors:
Wave Life Sciences Ltd.
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Solid cancers
Sponsors:
Yang Yang, MD, PhD, MSCR, The Affiliated Nanjing Drum Tower Hospital of Nanjing University Medical School
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Sponsors:
Huazhong University of Science and Technology
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Sponsors:
Huazhong University of Science and Technology
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Sponsors:
First Affiliated Hospital, Sun Yat-Sen University
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Sponsors:
First Affiliated Hospital of Guangdong Pharmaceutical University
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Sponsors:
The First Affiliated Hospital of Guangdong Pharmaceutical University
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Viral diseases
Sponsors:
Affiliated Hospital to Academy of Military Medical Sciences
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Sponsors:
Mahmoud Ramadan mohamed Elkazzaz
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Other rare inherited blood disorders
Sponsors:
Shanghai Children's Medical Center
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Other rare inherited disorders
Long-term follow-up (LTFU) studies
Sponsors:
Editas Medicine, Inc.
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Sponsors:
Vertex Pharmaceuticals
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Sponsors:
Sangamo Therapeutics
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