A single intravenous dose of Intellia Therapeutics’ in vivo CRISPR-Cas9 therapy lonvoguran ziclumeran (lonvo-z) reduced monthly hereditary angioedema...
Updated phase 1 data indicate that a single infusion of Caribou Biosciences' CB-011, an allogeneic anti-BCMA CAR-T cell therapy, can induce deep and...
Researchers have developed a new prime-editing screening platform that substantially improves editing efficiency and enables large-scale functional...
Researchers have reported the first use of CRISPR-derived base editing to make precise DNA changes in human embryos while avoiding the large...
Early clinical results suggest that FT836, an off-the-shelf CAR T-cell therapy derived from induced pluripotent stem cells (iPSCs), may induce tumour...
AIRNA has taken a different route to correcting the genetic lesion behind alpha-1 antitrypsin deficiency (AATD). Its oligonucleotide AIR-001 restored...
Updated Phase 1 data presented at the 2026 American Society of Gene and Cell Therapy (ASGCT) meeting suggest that Fate Therapeutics’ off-the-shelf CAR...
A new regulatory framework proposed in February by the US Food and Drug Administration could dramatically reduce the time and cost of bringing...
