| CRISPR Medicine | This is an overview of our interviews
Hypertrophic cardiomyopathy (HCM) frequently causes sudden cardiac death, often with little or no warning. In a key paper, researchers at University...
In a recent study, researchers in Spain confirmed the feasibility of using CRISPR-Cas9 to correct pathogenic mutations in the ABCA4 gene in...
A Danish start-up, BioPhenyx, has developed a functional genetic assay that uses CRISPR to evaluate the effects of any mutation of interest. The...
Spinal muscular atrophy is a severe neuromuscular disease caused by mutations in the SMN1 gene. While a few therapies have been approved for SMA, none...
Researchers from Utah State University and Germany’s Helmholtz Institute for RNA-based Infection Research demonstrate that upon recognition of an RNA...
Founded in 2011, Caribou Biosciences is developing novel allogeneic CAR-T cell and CAR-natural killer cell therapies to treat cancer. The UC Berkeley...
Huntington’s disease is a fatal condition, and despite decades of research, there is no known cure. The patient community may now have new hope in the...
Professor Stephanie Cherqui of University of California San Diego’s School of Medicine recently received a prestigious grant from the Californian...