The CRISPR gene-editing therapy more than doubled the lifespan in a mouse model by tackling the root cause of Hutchinson-Gilford progeria. The new...
In this roundup, we look back on our interviews with scientists who are making strides in developing CRISPR-based cures for genetic diseases.
CRISPR is believed to hold the cure for many rare single-gene disorders that are otherwise incurable. Alessia Cavazza’s group at University College...
CRISPR genome editing marches forward as a curative therapy for genetic disorders. Here lead scientist Ayal Hendel talks about how he is developing a...
Using 'dead' dCas9 fused to transcriptional activators researchers wake silent genes to alleviate blindness in a mouse model of retinitis pigmentosa -...
The first clinical trial results indicate that CRISPR is a safe and beneficial gene editing tool in humans. However, full therapeutic translation of...
By combining peptide display and different AAV serotypes, researchers have learned how to make and identify viral vectors that can target and...
Gene therapy stops deadly chemical warfare nerve agents in mice. The new research could lead to long-lasting protection by arming mice with...