Adeno-associated virus (AAV)

Adeno-associated virus (AAV)

Hemophilia B, (NCT06379789)
Sponsors:
Regeneron Pharmaceuticals
IndicatorIndicator
IND Enabling
Phase I
Phase II
Phase III
Indicator
IND Enabling
Phase I
Phase II
Phase III
IndicatorIndicator
IND Enabling
Phase I
Phase II
Phase III
Congenital Hearing Loss, (NCT06025032)
Sponsors:
HuidaGene Therapeutics Co., Ltd.
Indicator
IND Enabling
Phase I
Phase II
Phase III
Severe Pyruvate Kinase Deficiency, PKD, (ChiCTR2300073795)
Sponsors:
Shanghai Children's Medical Center
Indicator
IND Enabling
Phase I
Phase II
Phase III
IND Enabling
Phase I
Phase II
Phase III
Duchenne Muscular Dystrophy, DMD, (NCT05514249)
Sponsors:
Cure Rare Disease, Inc
Indicator
IND Enabling
Phase I
Phase II
Phase III
Retinitis Pigmentosa, RP, (NCT05805007)
Sponsors:
Peking University Third Hospital
Indicator
IND Enabling
Phase I
Phase II
Phase III
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