Researchers in the US, Japan and the UK report in Nature Biotechnology that genome editing with Cas9 and adeno-associated virus repair templates leads...

HuidaGene Therapeutics recently announced that the FDA has granted Orphan Drug Designation to its CRISPR-based therapeutic candidate, HG302. The...

Researchers report the treatment of a genetic liver disease in mice through transient prime editor expression.

Gene-editing systems, especially CRISPR-Cas9, have revolutionised genome editing, offering potential cures for genetic disorders, cancers, and other...

AAV trailblazer Nicole Paulk, formerly of UCSF, speaks about the latest developments in AAV-based gene therapies and her new company, Siren...

Excision BioTherapeutics reported positive interim clinical data for its HIV therapeutic candidate EBT-101 at this year's European Society for Gene &...

There are currently four clinical-stage gene-editing candidates in clinical trials for sickle cell disease, which affects millions of people worldwide...

A one-shot CRISPR cure for HIV may be in sight with a new approach that eliminated replication-competent virus in 58% of infected mice. The method...