CRISPR gene editing can lead to integration of mitochondrial DNA (mtDNA) fragments into the nuclear genome, raising potential safety concerns in...

Delivering mRNA via acid-degradable nanoparticles offers a new frontier in prenatal gene editing, setting the stage for treatments targeting the root...

In a move to potentially treat blindness, researchers have used CRISPR-Cas9 technology to permanently disrupt VEGFA expression in the eyes of rhesus...

Researchers in South Korea have introduced a novel microfluidic platform, termed Droplet Cell Pincher (DCP), to enhance CRISPR-Cas9 genome editing....

Researchers have developed a novel strategy to treat spinal muscular atrophy (SMA) by combining gene supplementation with CRISPR genome editing. The...

In a new breakthrough, researchers have achieved significant advances in gene editing of lung stem cells, demonstrating the potential for durable...

Researchers in the US, Japan and the UK report in Nature Biotechnology that genome editing with Cas9 and adeno-associated virus repair templates leads...

Located in the ETH Innovation & Entrepreneurship Lab in Zürich (Switzerland), Ariya Bio's goal is to develop safe and effective gene-editing therapies...