Scientists engineered ultrasound-controlled CRISPR tools that can precisely edit genes deep within tissues, demonstrating successful gene regulation...
Researchers in Korea report that large DNA deletions occur during DNA repair at a much lower frequency for base editors and prime editors than for...
Researchers in the US report a potentially new therapeutic strategy for amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD). Using...
Researchers in France report the correction of three duplications in the dystrophin gene in cells from Duchenne muscular dystrophy patients, using...
In a hunt for ways to improve the efficiency of CRISPR–Cas9-mediated homologous recombination, researchers find that a single exonuclease, TREX1,...
In an article published in Molecular Therapy, researchers at Rush University Medical Center in Chicago report that simultaneous Sox9 activation and...
In a new breakthrough, researchers have achieved significant advances in gene editing of lung stem cells, demonstrating the potential for durable...
Researchers at various institutions in the United States report genome editing in the lungs of young rhesus monkeys using CRISPR-Cas9 reagents...