Researchers in the US report a potentially new therapeutic strategy for amyotrophic lateral sclerosis (ALS) and frontotemporal dementia (FTD). Using...
Researchers in France report the correction of three duplications in the dystrophin gene in cells from Duchenne muscular dystrophy patients, using...
In a hunt for ways to improve the efficiency of CRISPR–Cas9-mediated homologous recombination, researchers find that a single exonuclease, TREX1,...
In an article published in Molecular Therapy, researchers at Rush University Medical Center in Chicago report that simultaneous Sox9 activation and...
In a new breakthrough, researchers have achieved significant advances in gene editing of lung stem cells, demonstrating the potential for durable...
Researchers at various institutions in the United States report genome editing in the lungs of young rhesus monkeys using CRISPR-Cas9 reagents...
Scientists in Italy have demonstrated that DNA base editing corrects common haemophilia A mutations and restores factor VIII expression in in vitro...
SNIPR Biome announced today that it has secured funding from CARB-X to further advance SNIPR001 into clinical trials in haematological cancer...