Delivering mRNA via acid-degradable nanoparticles offers a new frontier in prenatal gene editing, setting the stage for treatments targeting the root...

Dual CAR-T cells incorporating an IF/THEN logic-gated system show enhanced anti-tumour cytotoxicity and reduced off-tumour effects in mouse models....

Intellia Therapeutics announced yesterday that the UK’s Medicine and Healthcare products Regulatory Agency has cleared its clinical trial application...

Three research groups recently independently elucidated the genetic and epigenetic mechanisms driving prostate cancer metastasis. The innovative use...

Researchers in the US have demonstrated that a single local injection of lentiviral particles carrying Cas9 and a MYOC-targeting gRNA reverses disease...

Researchers report the treatment of a genetic liver disease in mice through transient prime editor expression.

Excision BioTherapeutics reported positive interim clinical data for its HIV therapeutic candidate EBT-101 at this year's European Society for Gene &...

There are currently four clinical-stage gene-editing candidates in clinical trials for sickle cell disease, which affects millions of people worldwide...