Delivering mRNA via acid-degradable nanoparticles offers a new frontier in prenatal gene editing, setting the stage for treatments targeting the root...

Italian scientists have demonstrated the potential of a targeted CRISPR-Cas9 delivery system to suppress tumour growth and metastasis in prostate...

In a new breakthrough, researchers have achieved significant advances in gene editing of lung stem cells, demonstrating the potential for durable...

Researchers report the treatment of a genetic liver disease in mice through transient prime editor expression.

Gene-editing systems, especially CRISPR-Cas9, have revolutionised genome editing, offering potential cures for genetic disorders, cancers, and other...

Verve Therapeutics has announced the first human proof-of-concept data demonstrating durable reductions in cholesterol for its in vivo base-editing...

Extended survival times and inhibited growth of patient-derived glioblastoma brain tumours have been achieved in mice with CRISPR-Cas9 mediated...

Most pharmaceuticals don't reach the brain, leaving cognitive impairments due to diseases like mucopolysaccharidoses (MPS) hard to treat. Now, a...