Researchers in Germany and Italy report the long-term effectiveness and safety of a CRISPR-Cas9 based approach known as homology-independent targeted...
Webinar
Read more about the webinar - Deliver CRISPR to the Brain - A New Treatment Strategy for Mucopolysaccharidoses
Most pharmaceuticals don't reach the brain, leaving cognitive impairments due to diseases like mucopolysaccharidoses (MPS) hard to treat. Now, a...
A recent proof-of-concept study from the Sontheimer lab at the University of Massachusetts Chan Medical School uses all-in-one, self-inactivating AAV...
CRISPR-based blood cell therapies are advancing through clinical trials, with promising results stacking up for certain rare genetic diseases and some...
