Beta Thalassemia
Beta Thalassemia
IND Enabling
Phase I
Phase II
Phase III
Transfusion-dependent Beta-Thalassemia, TDT, (NCT06065189)
Sponsors:
Children's Hospital of Fudan University![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Sponsors:
Children's Hospital of Fudan University
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
IND Enabling
Phase I
Phase II
Phase III
Transfusion-dependent Beta-Thalassemia, TDT, (NCT06291961)
Sponsors:
CorrectSequence Therapeutics Co., Ltd![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Sponsors:
CorrectSequence Therapeutics Co., Ltd
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
IND Enabling
Phase I
Phase II
Phase III
IND Enabling
Phase I
Phase II
Phase III
IND Enabling
Phase I
Phase II
Phase III
Transfusion-Dependent Beta-Thalassemia, TDT, (NCT06041620)
Sponsors:
Institute of Hematology & Blood Diseases Hospital, China![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Sponsors:
Institute of Hematology & Blood Diseases Hospital, China
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
IND Enabling
Phase I
Phase II
Phase III
Sickle Cell Disease, SCD, and Transfusion-Dependent Beta-thalassemia, TDT, (NCT05145062)
Sponsors:
Sangamo Therapeutics![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
Sponsors:
Sangamo Therapeutics
![CMN+](https://d2qa4785ekzzy0.cloudfront.net/fileadmin/templates/crisprmedicine/images/CMN-plus-list.png)
IND Enabling
Phase I
Phase II
Phase III
IND Enabling
Phase I
Phase II
Phase III