The US FDA has issued a Study May Proceed notification for PBGENE-DMD, Precision BioSciences' investigational in vivo gene-editing therapy for...

Dr. Cecilia Jimenez-Mallebrera, a leading neuromuscular disease researcher, examines how gene editing is progressing from the laboratory to clinical...

Researchers in the UK report a clinically-relevant transplantation strategy using CRISPR-corrected human myogenic cells in hydrogels that generate...

Some of the best links we picked up around the internet

A novel engineered TadA ortholog-derived cytosine base editor (aTdCBE) can overcome existing limitations in motif preferences and adenosine activity...

Researchers in France report the correction of three duplications in the dystrophin gene in cells from Duchenne muscular dystrophy patients, using...

HuidaGene Therapeutics recently announced that the FDA has granted Orphan Drug Designation to its CRISPR-based therapeutic candidate, HG302. The...

Folding DNA into compact structures allows for efficient integration of large genes, and this might lead to new therapies for genetic diseases with...