Researchers in Germany and Italy report the long-term effectiveness and safety of a CRISPR-Cas9 based approach known as homology-independent targeted...
In 2021, we've seen positive clinical data for the first ever in vivo CRISPR medicines, base editors are heading for the clinic, and CRISPR therapies...
A disease model using patients’ own cells demonstrates that prime editing can be used for functional repair of mutations leading to metabolic...
For the first time, scientists can use gene therapy to correct a diabetes-causing mutation in stem cells derived from patients. The edited stem cells...