HuidaGene Therapeutics recently announced that the FDA has granted Orphan Drug Designation to its CRISPR-based therapeutic candidate, HG302. The...
Folding DNA into compact structures allows for efficient integration of large genes, and this might lead to new therapies for genetic diseases with...
2021 was a very successful year for CRISPR in the medical field. Much of the success comes down to gene editing without double-strand breaks,...
In 2021, we've seen positive clinical data for the first ever in vivo CRISPR medicines, base editors are heading for the clinic, and CRISPR therapies...
Mammoth Biosciences was until recently most well known as a diagnostic company using CRISPR technology, but through a newly announced partnership with...
Webinar
Read more about the webinar - Rare Diseases & CRISPR
Contraction kinetics of isogenic myofibers before and after CRISPR correction are compared in a microdevice with a light pulse. The optogenetic model...
Editing a single nucleotide in the largest human gene is sufficient to restore dystrophin production and myocyte function in Duchenne muscular...
