Cas12

Cas12

Primary Hyperoxaluria Type 1, (NCT06839235)
Sponsors:
Arbor Biotechnologies
IndicatorIndicator
IND Enabling
Phase I
Phase II
Phase III
Duchenne Muscular Dystrophy, DMD, (NCT06594094)
Sponsors:
HuidaGene Therapeutics Co., Ltd.
IND Enabling
Phase I
Phase II
Phase III
Indicator
IND Enabling
Phase I
Phase II
Phase III
Transfusion-Dependent Beta-Thalassemia, TDT, (NCT06041620)
Sponsors:
Institute of Hematology & Blood Diseases Hospital, China
IND Enabling
Phase I
Phase II
Phase III
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