Scientists engineered nanoparticles capable of delivering genetic material to lung cells with high efficiency when administered intravenously. Based...
Jennifer Doudna and colleagues have engineered a thermostable Cas9 variant, iGeoCas9, which dramatically enhances genome editing efficiency in...
Researchers in South Korea have developed a cadmium selenide (CdSe) quantum dot (Qdot) system to deliver CRISPR-Cas9 for gene editing in microglia,...
A novel engineered TadA ortholog-derived cytosine base editor (aTdCBE) can overcome existing limitations in motif preferences and adenosine activity...
In a recent study, researchers in Italy addressed the critical need for experimental validation of durable epigenetic silencing after transient...
Intellia Therapeutics shares interim clinical results from the Phase 1 portion of the ongoing Phase 1/2 trial of NTLA-2002 in hereditary angioedema...
Verve Therapeutics has announced the first human proof-of-concept data demonstrating durable reductions in cholesterol for its in vivo base-editing...
By decorating lipid nanoparticles with a cell-specific surface marker, researchers from the University of Pennsylvania were able to edit...