When clinicians at the Children’s Hospital of Philadelphia (CHOP) treated baby KJ – born with a rare, often-fatal urea-cycle disorder – with a CRISPR...
Intellia Therapeutics has initiated a rolling biologics license application (BLA) with the U.S. Food and Drug Administration for lonvoguran ziclumeran...
A Chinese research team has developed TIGER (Template-Independent Genome Editing for Restoration), a CRISPR-Cas9 platform that corrects frameshift...
Some of the best links we picked up around the internet
Scribe Therapeutics is preparing to take its first cardiometabolic programme into the clinic in mid-2026, positioning STX-1150 as a potentially...
One or two years ago, if you had proposed lipid nanoparticles (LNPs) as an RNA delivery system for muscle diseases, you would likely have been met...
A novel genome-editing platform addresses one of the field's most constant challenges – how to insert kilobase-scale DNA into living cells without...
