Researchers in the US have demonstrated that a single local injection of lentiviral particles carrying Cas9 and a MYOC-targeting gRNA reverses disease...

AAV trailblazer Nicole Paulk, formerly of UCSF, speaks about the latest developments in AAV-based gene therapies and her new company, Siren...

Researchers at Ulsan National Institute of Science and Technology in South Korea have developed a CRISPR-Cas9-based method to eliminate tumour cells....

This week's update includes news about two gene-edited therapies for cancer. Allogene Therapeutics' ALLO-316 has been granted Fast Track Designation...

Intellia Therapeutics recently announced that the first patient had been dosed in its Phase 1/2a CRISPR trial for acute myleoid leukaemia (AML). The...

For the first time, a team of scientists and medical doctors in Germany is exploring CRISPR to treat the rare genetic disorder Metachromatic...

Researchers at Texas Biomedical Research Institute in San Antonio, Texas have developed a novel strategy to inhibit human immunodeficiency virus (HIV)...

Base editors are derived from CRISPR-Cas technology and have the potential to cure many genetic diseases by precisely correcting single pathogenic...